By attacking and further understanding genetics, stem cell research, cellular biology and basic science, we can now 1) identify and create better ALS drugs to test, and 2) better assess these drugs through improved tests and models of the disease. While scientists’ approach to ALS drug testing was once “a shot in the dark”, Project ALS researchers now have the knowledge and technology to more comprehensively and accurately test promising drugs at the pre-clinical level, and subsequently, in human clinical trial.

NextGen ALS: A Weber Family Initiative
In 2020, Cathy and Richard called Project ALS after hearing about the development of a novel antisense oligonucleotide (ASO) therapy for people living with FUS ALS. So was born NextGen ALS, a Weber family initiative in collaboration with Project ALS that is committed to raising funds for targeted research toward treatments and cures for genetic forms of ALS.